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Phase Ill, open-label, single-dose, multi-center multinational trial investigating a serotype 5 adeno-associated viral vector containing the Padua variant of a codon-optimized human factor IX gene (AA VS-hFIXco-Padua, AMT-061) administered
Kotowski, Adam
(PI)
University At Buffalo
Project
:
Research
Overview
Project Details
Status
Finished
Effective start/end date
05/1/19
→
12/31/23
Funding
uniQure Biopharma BV:
$59,648.00
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